United KingdomResearch and clinical trials
Stem cell transplant in chronic granulomatous disease in the long term: high survival, frequent late effects
A study published in a journal and reviewed by independent scientists. Even so, a single study is not conclusive; it needs to be replicated.
In London, 42 children who had a stem cell transplant for chronic granulomatous disease were studied. The transplants were done between 1994 and 2020, and the children were followed for at least two years. The ten-year survival rate was 95%. One-third of the children developed problems in which the immune system attacks the body's own tissues. Late effects such as excess weight, mental health problems and hormone problems were also seen.
What does it mean for patients and families?
Even when the transplant is successful, the children need to be followed for years by different specialists.
Source
Scientific paper: Beyond survival: Multisystem long-term outcomes following HSCT in chronic granulomatous disease. Journal of Human Immunity, 2026. DOI: 10.70962/jhi.20250076 · PubMed 42170327
The source page was opened and read on October 7, 2026. Summary prepared by the Doktorclub editorial team and translated from Turkish; it has not yet been reviewed by a physician (a scientific board is being set up).
This page is translated from the Turkish original.
Related disease: Chronic granulomatous disease (CGD)
This page reports a development; it is not a treatment recommendation. Your doctor decides whether a treatment is right for you.